Prilenia, a clinical stage biotechnology company focused on the urgent mission to develop novel therapeutics to slow the progression of neurodegenerative diseases and neurodevelopmental disorders, has filed a European Marketing Authorization Application (MAA) with the European Medicines Agency (EMA) for Baca lebih lanjut...
I belong to the third generation of a family affected by Huntington’s Disease, but it wasn’t until 2024, thanks to the tireless efforts of my second father, F. Cook, that we were able to confirm how the disease entered the Baca lebih lanjut...
Abu Dhabi, UAE; June 19, 2024: IROS, an Abu Dhabi-based contract research organization (part of the M42 group), has partnered with Prilenia Therapeutics, a clinical-stage biotech company, and the International Huntington’s Disease Association (IHA) to plan the first-ever clinical trial Baca lebih lanjut...
“We are very pleased with these new data demonstrating a statistically significant, dose-dependent slowing of the progression of Huntington’s disease and lowering of NfL in the CSF at 24 months,” stated Walid Abi-Saab, M.D., chief medical officer of uniQure. “We believe Baca lebih lanjut...
Today, Wave Life Sciences announced positive results from SELECT-HD, our Phase 1b/2a placebo-controlled trial evaluating the investigational therapy WVE-003. These results demonstrate that WVE-003 selectively lowers toxic, mutant huntingtin (mHTT) protein and preserves healthy, wild-type huntingtin (wtHTT) protein for individuals Baca lebih lanjut...
At Month 12, mutant Huntingtin (mHTT) in the blood was lowered by 22% and 43% respectively for 5mg and 10mg doses. A similar result was seen in cerebrospinal fluid, where mHTT was lowered by 21% and 43% respectively, for 5mg Baca lebih lanjut...
Earlier this week Sage Therapeutics announced the results of their SURVEYOR study which quantified the cognitive impact of Huntington’s Disease. Using the HD-Cognitive Assessment Battery (HD-CAB) they measured the difference between 29 healthy volunteers and 40 participants with HD. As Baca lebih lanjut...
Presiden IHA, Svein Olaf Olsen, menjadi pembicara utama tentang Penyakit Huntington di Kongres MENA untuk Penyakit Langka di Abu Dhabi bulan lalu. Beliau berbicara tentang kebutuhan mendesak untuk mendirikan pusat keunggulan neurodegeneratif di wilayah ini dan Baca lebih lanjut...
Hari ini kami sangat bahagia di komunitas Huntington. Pengumuman dari Uniqure bahwa perusahaan telah menerima Regenerative Medicine Advanced Therapy (RMAT) "Penunjukan untuk Terapi Gen Investigasi AMT-130 pada Penyakit Huntington lebih dari sekadar menjanjikan", kata Presiden Baca lebih lanjut...
Dalam memoarnya "We Exist", Tanita Allen menceritakan kesulitan yang dialaminya untuk mendapatkan gejala yang didiagnosis dengan benar sebagai Penyakit Huntington. Berkali-kali, dia salah didiagnosis karena dokter menolak untuk mempertimbangkan bahwa orang Afrika-Amerika juga dapat mewarisi mutasi Baca lebih lanjut...
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