PTCセラピューティクス社、ハンチントン病患者を対象としたPIVOT-HD臨床試験の良好な中間データを発表

June 21, 2023 PDF Version – Dose-dependent lowering of blood Huntingtin (HTT) protein levels at 12 weeks –– Favorable tolerability profile with no treatment-related serious adverse events or NfL spikes –  – Conference call and webcast to be held June 21st at 8:00 am EDT –  SOUTH 続きを読む...

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