PTC šodien paziņoja daudzsološus 12 mēnešu rezultātus no 2. fāzes PIVOT-HD pētījuma par perorālo PTC518.
At Month 12, mutant Huntingtin (mHTT) in the blood was lowered by 22% and 43% respectively for 5mg and 10mg doses. A similar result was seen in cerebrospinal fluid, where mHTT was lowered by 21% and 43% respectively, for 5mg Lasīt vairāk...