Categorie: Nieuws

IROS, Prilenia en de Internationale Vereniging voor de Ziekte van Huntington werken samen aan het allereerste onderzoek naar de ziekte van Huntington (HD) in de MENA-regio

Abu Dhabi, UAE; June 19, 2024: IROS, an Abu Dhabi-based contract research organization (part of the M42 group), has partnered with Prilenia Therapeutics, a clinical-stage biotech company, and the International […]

uniQure kondigt positieve tussentijdse data-update aan die de vertraging van de ziekteprogressie aantoont in fase I/II-onderzoek naar AMT-130 voor HD

“We are very pleased with these new data demonstrating a statistically significant, dose-dependent slowing of the progression of Huntington’s disease and lowering of NfL in the CSF at 24 months,” […]

Wave Life Sciences kondigt positieve resultaten aan van fase 1b/2a SELECT-HD-trial met de eerste klinische demonstratie van allelselectieve verlaging van mutant-Huntingtine bij de ziekte van Huntington

Today, Wave Life Sciences announced positive results from SELECT-HD, our Phase 1b/2a placebo-controlled trial evaluating the investigational therapy WVE-003. These results demonstrate that WVE-003 selectively lowers toxic, mutant huntingtin (mHTT) […]

PTC kondigde vandaag veelbelovende 12-maandenresultaten aan van hun Fase 2 PIVOT-HD-studie met oraal PTC518  

At Month 12, mutant Huntingtin (mHTT) in the blood was lowered by 22% and 43% respectively for 5mg and 10mg doses. A similar result was seen in cerebrospinal fluid, where […]

Fase 2-studie van Sage Therapeutics bevestigt de cognitieve impact van de ziekte van Huntington

Earlier this week Sage Therapeutics announced the results of their SURVEYOR study which quantified the cognitive impact of Huntington’s Disease.  Using the HD-Cognitive Assessment Battery (HD-CAB) they measured the difference […]

Update uit het Midden-Oosten en Noord-Afrika

IHA President Svein Olaf Olsen was keynote speaker on Huntington’s Disease at the MENA Congress for Rare Diseases in Abu Dhabi last month. He spoke of the urgent need to […]

FDA kent uniQure Regenerative Medicine Advance Therapy (RMAT)-status toe

Vandaag zijn we erg blij in de Huntington gemeenschap. De aankondiging van Uniqure dat het bedrijf de Regenerative Medicine Advanced Therapy (RMAT) "Designation for Investigational Gene Therapy AMT-130 [...]

Gratis online psychotherapieprogramma voor mensen met HD

Doctors at the University of Reading (UK) have developed a free online psychotherapy programme for people with Huntington’s Disease.  It’s part of a research project that looks at how people […]

Een nieuwe vereniging voor de Ziekte van Huntington wordt gefinancierd in Pakistan - HDSOP

Founding of the Huntington’s Disease Society of Pakistan April 24th 2024 Last week another national association was created.  The Huntington’s Disease Society of Pakistan (HDSOP) joined the growing  list of […]

SOM Biotech rondt het rekruteringsproces af in de Fase IIb studie naar de behandeling van chorea bij de ziekte van Huntington

SOM Biotech, a clinical-stage drug discovery and development company based on a unique proprietary Artificial Intelligence platform (SOMAIPRO®), is pleased to announce that the recruitment of the Phase IIb clinical […]